Search for Clinical and Behavioral Research Studies

Ann & Robert H. Lurie Children’s Hospital of Chicago and Stanley Manne Children’s Research Institute lead or participate in hundreds of research studies that seek answers about diseases, better treatments, preventative care, and more. Many of these studies can be found in this database. Use the finder to learn more. 
 

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Showing 1 - 10 of 31 results
Matching clinical studies
Study Title Keywords Status
Study Title
ID: NCT05693142 PI: Nancy L Kuntz
AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
Keywords
Muscular Dystrophies
dmd
Status
Recruiting
Study Title
ID: NCT05881408 PI: Nancy L Kuntz
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) in Non-Ambulatory and Ambulatory Participants With Duchenne Muscular Dystrophy (DMD)
Status
Recruiting
Study Title
ID: NCT05374590 PI: Nancy L Kuntz
Evaluating Long-term Safety of Efgartigimod Administered Intravenously and Efgartigimod PH20 Administered Subcutaneously in Children With Generalized Myasthenia Gravis
Keywords
myasthenia gravis
Status
Recruiting
Study Title
ID: NCT05808764 PI: Nancy L Kuntz
A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy
Status
Recruiting
Study Title
ID: NCT05004129 PI: Nancy L Kuntz
Safety and Efficacy of Tideglusib in Congenital Myotonic Dystrophy
Keywords
Muscular Dystrophies
congenital myotonic dystrophy
Status
Recruiting
Study Title
ID: NCT03532542 PI: Nancy L Kuntz
An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy
Status
Study Title
ID: NCT04488133 PI: Nancy L Kuntz
A Study of Nusinersen Among Participants With Spinal Muscular Atrophy Who Received Onasemnogene Abeparvovec
Status
Recruiting
Study Title
ID: NCT04089566 PI: Nancy L Kuntz
Study of Nusinersen (BIIB058) in Participants With Spinal Muscular Atrophy
Status
Recruiting
Study Title
ID: NCT04042025 PI: Nancy L Kuntz
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
Status
Study Title
ID: NCT05156320 PI: Nancy L Kuntz
Efficacy and Safety of Apitegromab in Patients With Later-Onset Spinal Muscular Atrophy Treated With Nusinersen or Risdiplam
Status
Recruiting