Search for Clinical and Behavioral Research Studies

Ann & Robert H. Lurie Children’s Hospital of Chicago and Stanley Manne Children’s Research Institute lead or participate in hundreds of research studies that seek answers about diseases, better treatments, preventative care, and more. Many of these studies can be found in this database. Use the finder to learn more. 
 

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Showing 11 - 20 of 33 results
Matching clinical studies
Study Title Keywords Status
Study Title
ID: NCT05693142 PI: Nancy L Kuntz
AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD)
Keywords
Muscular Dystrophies
dmd
Status
Recruiting
Study Title
ID: NCT05808764 PI: Nancy L Kuntz
A Study to Investigate the Pharmacokinetics and Safety of Risdiplam in Infants With Spinal Muscular Atrophy
Status
Recruiting
Study Title
ID: NCT05374590 PI: Nancy L Kuntz
Evaluating Long-term Safety of Efgartigimod Administered Intravenously and Efgartigimod PH20 Administered Subcutaneously in Children With Generalized Myasthenia Gravis
Keywords
myasthenia gravis
Status
Recruiting
Study Title
ID: NCT03863119 PI: Nancy L Kuntz
Expanded Access Protocol for Boys With Duchenne Muscular Dystrophy
Keywords
Muscular Dystrophies
Status
Not Recruiting
Study Title
ID: NCT02386553 PI: Nancy L Kuntz
A Study of Multiple Doses of Nusinersen (ISIS 396443) Delivered to Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy
Status
Not Recruiting
Study Title
ID: NCT02052791 PI: Nancy L Kuntz
An Open-label Safety and Tolerability Study of Nusinersen (ISIS 396443) in Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in ISIS 396443-CS2 (NCT01703988) or ISIS 396443-CS10 (NCT01780246)
Status
Not Recruiting
Study Title
ID: NCT03675126 PI: Nancy L Kuntz
An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP-5051
Status
Not Recruiting
Study Title
ID: NCT03381729 PI: Nancy L Kuntz
Study of Intrathecal Administration of Onasemnogene Abeparvovec-xioi for Spinal Muscular Atrophy
Status
Not Recruiting
Study Title
ID: NCT03199469 PI: Nancy L Kuntz
Gene Transfer Clinical Study in X-Linked Myotubular Myopathy
Status
Not Recruiting
Study Title
ID: NCT05096221 PI: Nancy L Kuntz
A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of SRP-9001 (Delandistrogene Moxeparvovec) in Participants With Duchenne Muscular Dystrophy (DMD)
Status
Not Recruiting