Abstract
The ONYX study is an Open-Label, Multicenter, Extension study that will evaluate the
long-term safety and efficacy of Apitegromab in Patients with Type 2 and Type 3 SMA who have
completed TOPAZ or SAPPHIRE.
Stanley Manne Children's Research Institute
Louis A. Simpson and Kimberly K. Querrey Biomedical Research Center
303 East Superior Street
Chicago, IL 60611
