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Impact of long-term elosulfase alfa on activities of daily living in patients with Morquio A syndrome in an open-label, multi-center, phase 3 extension study

Christian J. Hendriksz, Barbara K. Burton, Celeste Decker, Derralynn A. Hughes, Fiona J. Stewart, John J. Mitchell, Julian Raiman, Moeenaldeen D. AlSayed, Norberto Guelbert, Paul R. Harmatz, Robert Matousek, Roberto Giugliani, Rossella Parini, Sara M. Hawley