Clinical Trial
Lennox-Gastaut syndrome is a serious and rare form of epilepsy that begins in infancy and
early childhood. Seizures and their consequences need medical attention, emergency
Clinical Trial
The goal of Parts A and B of this Phase 1, first-in-human, randomized study is to assess the
safety, tolerability, and pharmacokinetics (PK) of single (SAD) and multiple (MAD)
Clinical Trial
This is a randomized, double-blind, placebo controlled, multicenter study to compare the
efficacy and safety of L-citrulline versus placebo in patients undergoing surgery for
Clinical Trial
This post-trial access program is to allow continued access for people who participated and
are benefitting from treatment on the HGT-HIT-046 (NCT01506141) or SHP609-302 (NCT02412787)
Clinical Trial
This trial is a multi-center, non-randomized, open-label Phase I/II study evaluating the
feasibility and efficacy of vincristine, irinotecan, temozolomide, and atezolizumab in
Clinical Trial
The primary purpose of this study is to assess the efficacy and safety of daily DBV712 250
micrograms (mcg) to induce desensitization to peanut in peanut-allergic children 4-7 years
Clinical Trial
The goal of this trial is to learn how well Setmelanotide works to improve weight reduction,
hunger, and quality of life in patients 4 years of age and older with acquired
Clinical Trial
The main objective of this trial is to evaluate the safety, tolerability, and pharmacodynamic
activity of BBP-812, an investigational AAV9-based gene therapy, in pediatric
Clinical Trial
This is an extension study to evaluate the long-term safety and efficacy of ligelizumab in
particiants who have completed a ligelizumab Phase III study in food allergy.
Clinical Trial
Tagraxofusp is a protein-drug conjugate consisting of a diphtheria toxin redirected to target
CD123 has been approved for treatment in pediatric and adult patients with blastic
Clinical Trial
This is an 18-month, multicenter, randomized, active-control, parallel-group Phase 3 study,
in which participants will be randomized to venglustat versus standard of care therapy
Clinical Trial
HOPE-3 is a two cohort, Phase 3, multi-center, randomized, double-blind, placebo-controlled
clinical trial evaluating the efficacy and safety of a cell therapy called CAP-1002 in
