Search

Filters

Filters

Looking for a researcher?
Find a researcher

Looking for a clinical study?
Find a Clinical Study

Search Results List

Showing 1 - 12 of 30 results
Publication

Efficacy and Safety of Viltolarsen in Boys With Duchenne Muscular Dystrophy: Results From the Phase 2, Open-Label, 4-Year Extension Study.

Clemens, Paula R; Rao, Vamshi K; Connolly, Anne M; Harper, Amy D; Mah, Jean K; McDonald, Craig M; Smith, Edward C; Zaidman, Craig M; Nakagawa, Tomoyuki; Hoffman, Eric P

Publication

Longitudinal Assessment of Timed Function Tests Over Time in Ambulatory Individuals with SMA Treated with Nusinersen.

Krosschell, Kristin J; Brown, Laurey; Hoffman, Katie; Zumpf, Katelyn B; Munson, Hannah; Bidwell, Jessa; Schulte, Duncan P; Schwaede, Abigail N; Buehner, Amber N; DiDonato, Christine J; Kuntz, Nancy L; Rao, Vamshi K